A lung tropic AAV vector improves survival in a mouse model of surfactant B deficiency | Nature Communications
Selection of an Efficient AAV Vector for Robust CNS Transgene Expression - ScienceDirect
Biomolecules | Free Full-Text | Optimized AAV Vectors for TMC1 Gene Therapy in a Humanized Mouse Model of DFNB7/11
Gene Therapy Preserves Retinal Structure and Function in a Mouse Model of NMNAT1-Associated Retinal Degeneration. - Abstract - Europe PMC
JCI Insight - Efficacy of AAV9-mediated SGPL1 gene transfer in a mouse model of S1P lyase insufficiency syndrome
Innate and adaptive AAV-mediated immune responses in a mouse model of Duchenne muscular dystrophy: Molecular Therapy - Methods & Clinical Development
Split AAV-Mediated Gene Therapy Restores Ureagenesis in a Murine Model of Carbamoyl Phosphate Synthetase 1 Deficiency: Molecular Therapy
AAV‐mediated delivery of an anti‐BACE1 VHH alleviates pathology in an Alzheimer's disease model | EMBO Molecular Medicine
Gaia Trincucci on X: "🐭New AAV-hACE2 mouse model of #SARSCoV2 infection from @VirusesImmunity, @benisraelow, @ericsongg & colleagues @YaleIBIO @YaleMed. Interesting insights on the role of Type I IFNs & lung pathology! https://t.co/W6EYxnq6rg #
Adeno‐associated virus‐based Alzheimer's disease mouse models and potential new therapeutic avenues - Ittner - 2019 - British Journal of Pharmacology - Wiley Online Library
Frontiers | Adeno-Associated Virus Technologies and Methods for Targeted Neuronal Manipulation
Hardwiring tissue-specific AAV transduction in mice through engineered receptor expression | Nature Methods
Controlling AAV receptor expression to improve testing and validation of AAV gene therapy products | Explore Technologies
Adeno-associated virus effectively mediates conditional gene modification in the brain | PNAS
AAV-Mediated Astrocyte-Specific Gene Expression under Human <i>ALDH1L1</i> Promoter in Mouse Thalamus
A Single Intravenous Injection of AAV-PHP.B-hNDUFS4 Ameliorates the Phenotype of Ndufs4−/− Mice - ScienceDirect
Ai9 Cre Reporter Mouse Strain and Study Plans for AAV Local and... | Download Scientific Diagram
AAV Gene Therapy Prevents and Reverses Heart Failure in a Murine Knockout Model of Barth Syndrome | Circulation Research
Standard screening methods underreport AAV-mediated transduction and gene editing | Nature Communications
AAV‐delivered diacylglycerol kinase DGKk achieves long‐term rescue of fragile X syndrome mouse model | EMBO Molecular Medicine
Rapid generation of mouse model for emerging infectious disease with the case of severe COVID-19 | PLOS Pathogens
Neonatal AAV gene therapy rescues hearing in a mouse model of SYNE4 deafness | EMBO Molecular Medicine
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders | Science Advances
AAV vector-mediated expression of foreign gene in mouse brain. a The... | Download Scientific Diagram
Frontiers | SEMMs: Somatically Engineered Mouse Models. A New Tool for In Vivo Disease Modeling for Basic and Translational Research
Experimental Variables that Affect Human Hepatocyte AAV Transduction in Liver Chimeric Mice - ScienceDirect
AAV-PHP.B-Mediated Global-Scale Expression in the Mouse Nervous System Enables GBA1 Gene Therapy for Wide Protection from Synucleinopathy - ScienceDirect
Frontiers | AAV Delivery of shRNA Against TRPC6 in Mouse Hippocampus Impairs Cognitive Function
